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type1.science

Potential cures and treatments

Therapies aiming to restore endogenous insulin production.

Approaches across cell replacement, immune protection, gene editing, and regeneration — each scored 0–100 against published, category-specific criteria, including insulin independence, durability, immunosuppression burden, and clinical maturity. Every row shows where it sits in the pipeline, when and where it may be available, and the headline result. Expand for the full scorecard and primary sources.

27 treatments  ·  reviewed Jun 2026
01
Stem-cell-derived islets (zimislecel / VX-880)Cell replacementEarly evidence

Closest to a functional cure. Lab-grown islet cells infused into the liver — the strongest cure proof of concept yet.

Pipeline

Phase 3

Available

Filing ~2026

Where

US · EU trials

Headline result

83% insulin-free at 1 year

55
Details +
02
Sana Biotechnology SC451 (hypoimmune stem-cell islets)Gene-editedEarly evidence

A cure without anti-rejection drugs — unproven. Stem-cell islets gene-edited to be invisible to the immune system — no anti-rejection drugs.

Pipeline

Preclinical

Available

Years away

Where

US (platform)

Headline result

C-peptide 12+ mo, drug-free (n=1)

50
Details +
03
Donor islet transplant (Lantidra / donislecel)Cell replacementRegulator-approved

A real cure, for a lucky few. Islet cells from deceased donors, infused into the liver — the first approved cell therapy for T1D.

Pipeline

Approved

Available

Available now

Where

US (FDA 2023)

Headline result

First FDA-approved cell therapy

49
Details +
04
Sernova Cell Pouch Bio-hybrid Organ (immunoprotected)EncapsulationPreclinical

Promising on paper; mice so far. An implantable, retrievable pouch that shields lab-grown islets from immune attack.

Pipeline

Preclinical

Available

Years away

Where

Lab (mice)

Headline result

100+ days drug-free (in mice)

46.25
Details +
05
Encellin thin-film cell encapsulation (ENCRT / ENC-201)EncapsulationPreclinical

Drug-free by design; very early. An ultrathin, retrievable film pouch that protects islet cells under the skin.

Pipeline

Phase 1

Available

Years away

Where

US (Phase 1)

Headline result

Non-fibrotic at 4 mo (human explant)

45.75
Details +
06
Repeat BCG vaccinationImmunotherapyEarly evidence

Repeated Bacillus Calmette-Guerin vaccination repurposed as immune/metabolic therapy for established T1D.

Pipeline

Phase 1

Available

Years away

37.5
Details +
07
Vertex/CRISPR VCTX211 (CRISPR hypoimmune islets)Gene-editedEarly evidence

Bold idea, trial halted. CRISPR-cloaked islet cells designed to survive without immunosuppression.

Pipeline

Phase 1

Available

Halted 2025

Where

Discontinued

Headline result

Phase 1 ended early (2025)

36.5
Details +
08
Stem Cell Educator therapyImmunotherapyEarly evidence

A dialysis-like procedure that circulates a person's blood through a device where their immune cells are briefly co-cultured with cord-blood-derived stem cells, then returned — aim

Pipeline

Phase 1

Available

Years away

35.3
Details +
09
Vertex VX-264 (device-encapsulated stem-cell islets)EncapsulationEarly evidence

A clear lesson in what doesn't work yet. Encapsulated stem-cell islets — proved safe drug-free, but the cells did not produce enough insulin.

Pipeline

Phase 1/2

Available

Discontinued

Headline result

Discontinued, Mar 2025

35.25
Details +
10
Beta-O2 ßAir bioartificial pancreas (oxygen-refueled macrocapsule)EncapsulationEarly evidence

A macroencapsulation device that addresses encapsulation's classic weakness — oxygen starvation — by building in a refillable oxygen tank that is topped up daily.

Pipeline

Phase 1

Available

Years away

Where

EU · OTHER

35
Details +
11
OPF-310 encapsulated porcine isletsEncapsulationEarly evidence

First-in-human xenotransplant program using encapsulated neonatal pig islet cells for adults with unstable T1D and repeated severe hypoglycemia despite closed-loop therapy.

Pipeline

Phase 1

Available

Years away

34.25
Details +
12
Autologous polyclonal Treg therapy (T-Rex program)ImmunotherapyModerate evidence

This approach takes a person's own regulatory T cells (Tregs) — the immune cells that normally keep autoimmunity in check — grows them into the billions in a lab, and infuses them

Pipeline

Phase 2

Available

Years away

32.9
Details +
13
Beta-cell regeneration / regrowth agentsRegenerationPreclinical

Regrow your own cells — still in the lab. Drugs that coax the body to regrow its own insulin-producing cells instead of transplanting new ones.

Pipeline

Phase 1

Available

Years away

Where

US (early)

Headline result

4–7× beta-cell growth (in lab)

32
Details +
14
Kriya Therapeutics KRIYA-839 (AAV insulin + glucokinase gene therapy)Gene-editedPreclinical

A one-time gene therapy that turns a person's own thigh muscle into a glucose-responsive insulin factory.

Pipeline

Preclinical

Available

Years away

Where

US

28.5
Details +
15
GLP-1 drugs to rescue beta cells at diagnosisRegenerationEarly evidence

GLP-1 receptor drugs — the semaglutide/tirzepatide family now famous for type 2 diabetes and weight loss — also protect and amplify beta cells in lab models.

Pipeline

Phase 1

Available

Years away

Where

US · UK · EU · CA · AU · JP

28.25
Details +
16
Remygen (oral GABA) — Diamyd's beta-cell regeneration betRegenerationModerate evidence

Remygen is Diamyd Medical's controlled-release oral form of GABA, a molecule that in lab and animal studies coaxes beta cells to multiply and calms islet inflammation.

Pipeline

Phase 2

Available

Years away

27.9
Details +
17
E-islet 01 allogeneic human regenerative isletsCell replacementEarly evidence

Early-stage; watch this space. Stem-cell-derived islets in an early trial for severe, long-standing T1D.

Pipeline

Phase 1/2a

Available

Years away

Where

China (trial)

Headline result

Phase 1/2a recruiting

26.5
Details +
18
Genprex GPX-002 (AAV Pdx1 + MafA alpha-to-beta reprogramming)Gene-editedPreclinical

An in-the-body gene therapy that aims to regrow insulin-making capacity without any transplant.

Pipeline

Preclinical

Available

Years away

Where

US

24
Details +
19
Dimethyl fumarate for beta-cell preservationImmunotherapyEarly evidence

A repurposed oral immunomodulator best known as the multiple-sclerosis drug Tecfidera, now being tested in Chinese phase 3 studies to see whether it can preserve C-peptide in adult

Pipeline

Phase 1

Available

On the horizon

23.4
Details +
20
GNTI-122 engineered Tregs (POLARIS)ImmunotherapyEarly evidence

A one-time autologous engineered regulatory T-cell therapy made from a person's own blood cells, designed to restore immune tolerance to pancreatic islets in recent-onset T1D.

Pipeline

Phase 1

Available

Years away

22
Details +
21
Denosumab beta-cell preservationRegenerationPreclinical

A repurposing hypothesis around denosumab, the RANKL-targeting osteoporosis drug, to protect or improve beta-cell function in early T1D.

Pipeline

Preclinical

Available

Years away

21.15
Details +
22
CELZ-201 perinatal tissue-derived cell therapyImmunotherapyEarly evidence

Very early; little to show yet. Perinatal-tissue cells infused into the pancreas just after a new diagnosis.

Pipeline

Phase 1/2a

Available

Years away

Where

US (trial)

Headline result

Phase 1/2a recruiting

20
Details +
23
IMMUNOSTEM PD-L1 HSPC gene therapyGene-editedPreclinical

A first-in-human gene-therapy program using a person's own CD34+ hematopoietic stem and progenitor cells, modified ex vivo with a lentiviral vector to express PD-L1 and re-establis

Pipeline

Preclinical

Available

Years away

18
Details +
24
NewcelX NCEL-101 / IsletRxCell replacementPreclinical

A pre-IND stem-cell-derived islet replacement program for insulin-dependent T1D, with NewcelX exploring combination immune protection using Eledon's anti-CD40L antibody tegoprubart

Pipeline

Preclinical

Available

Years away

16.1
Details +
25
Celregen CRG-002 iPSC-derived isletsCell replacementEarly evidence

Allogeneic iPSC-derived pancreatic islet cells being tested in an early exploratory China study for diabetes with hypoglycemia unawareness or severe hypoglycemic events.

Pipeline

Phase 1

Available

Years away

15.5
Details +
26
PIpepTolDC tolerogenic dendritic-cell vaccineImmunotherapyEarly evidence

A personalized immune-tolerance vaccine made from a person's own dendritic cells loaded with proinsulin peptide, being tested by City of Hope in a small phase 1 T1D safety/manufact

Pipeline

Phase 1

Available

Years away

13
Details +
27
Stem-cell-derived islet clusters (Seraxis SR-02)Cell replacementPreclinical

Seraxis SR-02 is allogeneic pancreatic endocrine cell clusters grown from a proprietary stem-cell line and implanted into the omentum (the fatty apron in the abdomen), where they a

Pipeline

Preclinical

Available

Years away

Where

US

12.5
Details +

Scores are a transparent 0–100 weighted average of published criteria — higher means closer to a durable cure for more people. Living with T1D, Preventing and Trials are ranked the same way. Science journalism, not medical advice.